Heredodegenerative Disorders, Nervous System - 25 Studies Found
Completed |
: Study of HuCNS-SC Cells in Patients With Infantile or Late Infantile Neuronal Ceroid Lipofuscinosis (NCL) : Neuronal Ceroid Lipofuscinosis : 2006-06-13 :
|
Completed |
: Genotype - Phenotype Correlations of LINCL :
: 2005-09-06 |
Active, not recruiting |
: Safety Study of a Gene Transfer Vector for Children With Late Infantile Neuronal Ceroid Lipofuscinosis :
: 2005-09-06 : Genetic: AAV2CUhCLN2 (3x10^12 particle units) gene transfer; one-time administration via neuro surgery p |
Completed |
: Cystagon to Treat Infantile Neuronal Ceroid Lipofuscinosis : Infantile Neronal Ceroid Lipofuscinosis : 2001-12-17 : Drug: Cystagon |
Recruiting |
: Study of ACE-083 in Patients With Charcot-Marie-Tooth Disease : Charcot-Marie-Tooth Disease : 2017-04-12 : Drug: ACE-083 Part 1 - Recombinant fusion protein. Part 2 - Recombinant fusion protein or buffer solutio |